Ann and Robert H. Lurie Children Hospital of Chicago

Chicago, Illinois 60611

1 studies enrolling now · 4 studies all time

What they study most

Muscular Atrophy, Spinal

Studies at this site

• A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy — Recruiting now
• A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy — Completed
• Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy — Completed
• An Expanded Access Program for Risdiplam in Participants With Spinal Muscular Atrophy (SMA) — APPROVED_FOR_MARKETING