Addenbrooke's Hospital, Cambridge University Hospitals NHS FT

Cambridge CB2 0QQ

2 studies enrolling now · 2 studies all time

What they study most

Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF), Hemophilia B

Studies at this site

• A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants, Adolescents and Adults With Hearing Loss Due to Otoferlin Mutations — Recruiting now
• A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B — Recruiting now